Cancer cells have ways to hide from the immune system, but there are some unique features on these dangerous cells that ...

Qatar has taken a landmark step in precision medicine after Sidra Medicine became the first hospital in the country — and one ...

For the millions of people living with genetic diseases like muscular dystrophy and inherited liver disorders, one of the ...

CRISPR functions as a programmable genetic memory system derived from bacterial immune defenses against viral infections. Guide RNA allows for rapid multiplexed targeting compared to older ...

Scientists are laying the groundwork for treating one of the most common genetic conditions in humans. Research out today ...

Through genome editing using CRISPR/Cas9, researchers stably create euglena mutants that can produce wax esters with improved cold flow, making the esters suitable as feedstock for biofuels. News ...

CHICAGO – A CRISPR-Cas9-based investigational therapy was linked with a drop in serum transthyretin (TTR) levels in patients with transthyretin amyloidosis with cardiomyopathy (ATTR-CM), according to ...

The gene editing treatment targets the relatively common 1717-1G>A splicing mutation, which does not respond to many current CF therapies.

Scientists have taken an important step toward a gene therapy that could one day turn off the extra genetic material that ...