Children with spinal muscular atrophy (SMA), a rare autosomal recessive disease that results in progressive muscle weakness and atrophy, can suffer the concerning consequences of dysphagia, which ...

Two children with a rare genetic condition will live very different lives because one was tested at birth and the other was ...

CAMBRIDGE, Mass., June 30, 2023 (GLOBE NEWSWIRE) -- Biogen Inc. (Nasdaq: BIIB) announced new SPINRAZA® (nusinersen) data aimed at answering critical questions for the spinal muscular atrophy (SMA) ...

FIREFISH Part 2 study met its primary endpoint by demonstrating a significant increase in motor milestones in infants aged 1-7 months after 12 months of treatment Large, pivotal global study confirms ...

-- Muscular Dystrophy Association Calls FDA Approval of Novartis' Itvisma (onasemnogene abeparvovec-brve) a Major Step Forward for the Spinal Muscular Atrophy Community Mary Fiance, National Vice ...

A new report provided updated figures estimated the birth prevalence of spinal muscular atrophy (SMA) in the US. Previous investigations revealed that SMA is diagnosed per every 1 in 10,000 births ...

When you buy through links on our articles, Future and its syndication partners may earn a commission. Stock image of a baby in the womb. An infant with spinal muscular atrophy was treated whilst ...

"The most apparent take-away from the study findings is that a model of developmental therapy focusing on frequency, intensity, and variability of activity, exercise, and self-driven exploration may ...

Biogen also reported new real-world evidence and progress on the development of a novel device to enhance the patient treatment experience CAMBRIDGE, Mass., June 30, 2023 (GLOBE NEWSWIRE) -- Biogen ...

A child was treated for a rare, potentially deadly genetic disorder while still in the womb — and now, she has survived past ...