The company has also received orphan drug, rare pediatric disease, and fast-track designations for LTS-101 as a potential treatment for the fatal neurodegenerative disease.

LTS-101 is a one-time AAV gene therapy candidate intended to provide durable expression of the TPP1 enzyme in the central nervous system (CNS) of children with CLN2 diseaseFDA designations underscore ...

Batten disease is a rare inherited condition that affects brain development and function. CLN3 disease is the most common type of this disease. The symptoms are life-changing. They usually begin ...

EDEN PRAIRIE, MN / ACCESS Newswire / October 16, 2025 / Helen’s Pink Sky Foundation will take center stage at one of the world’s premier sporting events this fall, with its logo set to appear on BWT ...

In Flint an early Saturday morning fire destroys the former Swansons Funeral Home. The Funeral Home was shutdown amid health code violations in 2017. A spokesperson for Slotkin said she was not home ...

A Spokane Valley family dealing with devastating diagnoses for two of their little boys has been dealt even more health challenges. 4 News Now featured the Tucker family in an article 2 years ago.